Breadcrumb Home Videos Focus on Rare Disease: Decoding genomes, unlocking therapies (2019) Welcome Anna Greka Ó³»´«Ã½; Brigham and Women’s Hospital; Harvard Medical School Beyond the Diagnosis: Rare disease awareness and advocacy through art Suzanne Scott Beyond the Diagnosis From a child's fatal diagnosis to tailor-made treatment in one year Timothy Yu Boston Children’s Hospital; Harvard Medical School Julia Vitarello Mila's Miracle Foundation Precision medicine for rare disease Matt Might University of Alabama Q & A panel Moderator: Anna Greka, chair of Focus on Rare Disease Panelists: Timothy Yu, Julia Vitarello, Suzanne Scott and Matt Might Latest news News 06.15.2026 2026 Merkin Prize in Biomedical Technology awarded to pioneers of the modern cochlear implant News 06.15.2026 Scientists improve nearly every aspect of prime editing, moving it closer to treating more genetic diseases News 05.13.2026 Precision DNA editing targets root cause of severe childhood epilepsy in preclinical study News 05.01.2026 Single-molecule tracker illuminates workings of cancer-related proteins All news
News 06.15.2026 2026 Merkin Prize in Biomedical Technology awarded to pioneers of the modern cochlear implant
News 06.15.2026 Scientists improve nearly every aspect of prime editing, moving it closer to treating more genetic diseases
News 05.13.2026 Precision DNA editing targets root cause of severe childhood epilepsy in preclinical study