Breadcrumb Home Videos Focus on rare disease: Prime time — gene therapy for rare disorders (2021) Welcome Anna Greka, Ó³»´«Ã½, Brigham and Women’s Hospital, Harvard Medical School Polr3a Neonatal Progeroid Syndrome: A Medical Mystery Leslie Macari, parent of a rare disease patient Keynote Lecture Base Editing and Prime Editing: Genome Editing Without Double-Strand Breaks David Liu, Ó³»´«Ã½, Harvard University, HHMI Q&A panel Moderator: Anna Greka, Chair of Focus on Rare Disease Panelists: David Liu, Leslie Macari Latest news News 03.04.2026 Gut bacteria rewire fat tissue to burn more energy News 02.26.2026 Study reveals genetic balancing act between autoimmunity and cancer risk News 02.25.2026 Free genetic testing program aims to improve medical care across Alabama News 02.25.2026 Scientists sharpen genetic maps to help pinpoint DNA changes that influence human health traits and disease risk All news
News 02.25.2026 Scientists sharpen genetic maps to help pinpoint DNA changes that influence human health traits and disease risk