Breadcrumb Home Videos Focus on rare disease: Prime time — gene therapy for rare disorders (2021) Welcome Anna Greka, Ó³»´«Ã½, Brigham and Women’s Hospital, Harvard Medical School Polr3a Neonatal Progeroid Syndrome: A Medical Mystery Leslie Macari, parent of a rare disease patient Keynote Lecture Base Editing and Prime Editing: Genome Editing Without Double-Strand Breaks David Liu, Ó³»´«Ã½, Harvard University, HHMI Q&A panel Moderator: Anna Greka, Chair of Focus on Rare Disease Panelists: David Liu, Leslie Macari Latest news News 10.16.2025 Ó³»´«Ã½-Bayer collaboration leads to drug candidate for a hard-to-treat type of lung cancer News 10.15.2025 Ó³»´«Ã½ Clinical Labs sets new GUINNESS WORLD RECORDSâ„¢ title for fastest DNA sequencing technique News 10.08.2025 A pioneering effort in patient-partnered cancer research enters a new phase News 09.30.2025 Jason Buenrostro named core institute member at Ó³»´«Ã½ All news
News 10.16.2025 Ó³»´«Ã½-Bayer collaboration leads to drug candidate for a hard-to-treat type of lung cancer
News 10.15.2025 Ó³»´«Ã½ Clinical Labs sets new GUINNESS WORLD RECORDSâ„¢ title for fastest DNA sequencing technique