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Session 1: Next Generation Scalable Technology
Chair: John Doench

Harnessing Functional Genomics and Machine Learning for Rare Cancers 
Gabe Griffin 

Rapidly Identifying Drugs for Rare Disorders by Pooled Image-Based Profiling
JT Neal

Multiplexed Optical Pooled Screening for Proteinopathy Therapeutic Discovery
Matt Brown

We are excited to invite you to the second annual Ladder to Cures Symposium | Reaching New Heights whose goal is to share progress in scalable technologies and advances in biology leading to treatments and cures for patients with rare genetic diseases. This hybrid all-day event will be held on May 16th, 2025 in the Ó³»­´«Ã½ Auditorium and streamed online. Anyone with an interest in rare disease research is invited to attend.

Building on Ó³»­´«Ã½â€™s strengths of scaling scientific efforts to accelerate progress, this symposium will convene scientists, physicians, patients/patient-led foundations and advisors from the biopharma and regulatory space to join the conversation.

For more information visit: /L2C