Matuszek Å», Brown BL, Yrigollen CM, Keiser MS, Davidson BL. Current Trends in Gene Therapy to Treat Inherited Disorders of the Brain. Molecular therapy : the journal of the American Society of Gene Therapy. 2025. doi:10.1016/j.ymthe.2025.03.057
Publications
Matuszek Å», Brown BL, Yrigollen CM, Keiser MS, Davidson BL. Current Trends in Gene Therapy to Treat Inherited Disorders of the Brain. Molecular therapy : the journal of the American Society of Gene Therapy. 2025. doi:10.1016/j.ymthe.2025.03.057
Etxaniz U, Marks I, Albin T, et al. AOC 1044 induces exon 44 skipping and restores dystrophin protein in preclinical models of Duchenne muscular dystrophy. Nucleic acids research. 2025;53(6). doi:10.1093/nar/gkaf241
Etxaniz U, Marks I, Albin T, et al. AOC 1044 induces exon 44 skipping and restores dystrophin protein in preclinical models of Duchenne muscular dystrophy. Nucleic acids research. 2025;53(6). doi:10.1093/nar/gkaf241
Luo Y, Khan MO, Wen C, et al. FairDiffusion: Enhancing equity in latent diffusion models via fair Bayesian perturbation. Science advances. 2025;11(14):eads4593. doi:10.1126/sciadv.ads4593
Luo Y, Khan MO, Wen C, et al. FairDiffusion: Enhancing equity in latent diffusion models via fair Bayesian perturbation. Science advances. 2025;11(14):eads4593. doi:10.1126/sciadv.ads4593
Deng L, Tan KS. Decoding Blastocystis-Driven Mechanisms in Gut Microbiota and Host Metabolism. Advanced science (Weinheim, Baden-Wurttemberg, Germany). 2025:e2416325. doi:10.1002/advs.202416325
Deng L, Tan KS. Decoding Blastocystis-Driven Mechanisms in Gut Microbiota and Host Metabolism. Advanced science (Weinheim, Baden-Wurttemberg, Germany). 2025:e2416325. doi:10.1002/advs.202416325
Mishra S, Morshed N, Sidhu SB, et al. The Alzheimer’s Disease Gene SORL1 Regulates Lysosome Function in Human Microglia. Glia. 2025. doi:10.1002/glia.70009
Vinken M, Grimm D, Baatout S, et al. Taking the 3Rs to a higher level: Replacement and reduction of animal testing in life sciences in space research. Biotechnology advances. 2025:108574. doi:10.1016/j.biotechadv.2025.108574